Families living with Prader-Willi syndrome are changing how PWS is understood, studied, and treated.
Aardvark Therapeutics has announced an update to its Phase 3 HERO trial that will allow more children and families affected by Prader-Willi syndrome to participate.The trial evaluating ARD-101 will now allow children as young as 7 years old to enroll...
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While much of FPWR’s work starts with discovery research, our mission extends across the full drug development pathway, supporting progress from foundational science all the way to potential treatments for Prader-Willi syndrome (PWS).
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Soleno Therapeutics has published results from its pivotal Phase 3 clinical study of VYKAT™ XR (diazoxide choline extended-release tablets, DCCR) in The Journal of Clinical Endocrinology and Metabolism, a peer-reviewed journal for endocrine and metab...
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Every breakthrough, every milestone, and every step forward in 2025 had one thing in common: our community. Because supporters like you showed up. You shared your story. You asked others to stand with you. And it mattered.
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The Global PWS Registry is powered by the dedication of patients and families who share their PWS experiences. Each piece of data collected helps unlock insights that fuel scientific discoveries and treatment breakthroughs.
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Rhythm Pharmaceuticals has shared positive preliminary results from its exploratory Phase 2 trial of setmelanotide in people with PWS and announced, pending successful completion of this phase, plans to advance setmelanotide into a Phase 3 trial. Add...
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As we wrap up 2025, we’re celebrating a year shaped by real progress… scientific breakthroughs, new treatment pathways, and meaningful improvements in care for people with Prader-Willi syndrome (PWS) and Schaaf-Yang syndrome (SYS).
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Ready to put purpose in your steps? The Harvesting Hope Distance Challenge is back starting October 16! Whether you walk, run, or waddle, every step funds critical research for Prader-Willi and Schaaf-Yang syndromes. And the best part? Thanks to a ge...
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